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Emma Ciafaloni Selected Research

Dichlorphenamide (Daranide)

1/2021Long-term efficacy and safety of dichlorphenamide for treatment of primary periodic paralysis.
12/2019Efficacy and Safety of Dichlorphenamide for Primary Periodic Paralysis in Adolescents Compared With Adults.
4/2016Randomized, placebo-controlled trials of dichlorphenamide in periodic paralysis.

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Emma Ciafaloni Research Topics

Disease

13Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker)
01/2022 - 06/2004
10Myasthenia Gravis
12/2021 - 09/2003
5Spinal Muscular Atrophy (Progressive Muscular Atrophy)
07/2022 - 01/2018
3Scoliosis
01/2022 - 01/2018
3Paralysis (Palsy)
01/2021 - 04/2016
3Muscular Dystrophies (Muscular Dystrophy)
01/2018 - 06/2012
2Vomiting
01/2022 - 01/2021
2Cough
01/2022 - 03/2008
2Myotonia
02/2013 - 10/2012
1Respiratory Tract Infections (Respiratory Tract Infection)
01/2022
1Left Ventricular Dysfunction
10/2021
1Headache (Headaches)
01/2021
1Disease Progression
01/2021
1Thymoma (Thymic Carcinoma)
11/2020
1Dropped Head Syndrome
01/2020
1Infections
01/2020
1Amyotrophic Lateral Sclerosis (Lou Gehrig's Disease)
01/2020
1Neoplasms (Cancer)
01/2020
1Parkinson Disease (Parkinson's Disease)
01/2020
1Exanthema (Rash)
12/2019
1Cardiomyopathies (Cardiomyopathy)
08/2018
1Hypoventilation
10/2016
1Nondystrophic myotonia
10/2012
1Rare Diseases (Rare Disease)
10/2012
1Weight Gain
11/2010
1Muscular Diseases (Myopathy)
01/2010
1Chest Pain (Chest Pains)
01/2010
1Myocardial Ischemia (Ischemic Heart Diseases)
01/2010

Drug/Important Bio-Agent (IBA)

7Adrenal Cortex Hormones (Corticosteroids)IBA
01/2022 - 09/2010
6Prednisone (Sone)FDA LinkGeneric
01/2022 - 09/2010
6Cholinergic ReceptorsIBA
12/2021 - 11/2016
4nusinersenIBA
01/2020 - 01/2018
3DystrophinIBA
01/2021 - 06/2004
3Dichlorphenamide (Daranide)FDA Link
01/2021 - 04/2016
2GlucocorticoidsIBA
01/2022 - 01/2018
2deflazacortIBA
01/2022 - 09/2010
2margatoxinIBA
11/2020 - 01/2019
2SteroidsIBA
05/2018 - 01/2016
1Rituximab (Mabthera)FDA Link
12/2021
1eteplirsenIBA
01/2021
1Immunosuppressive Agents (Immunosuppressants)IBA
01/2020
1eculizumabFDA Link
12/2019
1Cholinesterase Inhibitors (Anticholinesterases)IBA
01/2019
1Edrophonium (Tensilon)FDA LinkGeneric
01/2019
1AutoantibodiesIBA
01/2017
1Phosphotransferases (Kinase)IBA
01/2017
1ChloridesIBA
02/2013
1SodiumIBA
02/2013
1Mexiletine (Mexitil)FDA LinkGeneric
10/2012
1Sodium Channels (Sodium Channel)IBA
10/2012
1Ion Channels (Ion Channel)IBA
10/2012
1N-desmethylstobadineIBA
10/2012
1DNA (Deoxyribonucleic Acid)IBA
11/2011
1Creatine Kinase (Creatine Phosphokinase)IBA
11/2011
1Hydroxychloroquine (Plaquenil)FDA LinkGeneric
01/2010
1ThalliumIBA
01/2010
1Adenosine (Adenocard)FDA LinkGeneric
01/2010
1Antimalarials (Antimalarial Agents)IBA
01/2010
1Troponin IIBA
01/2010
1Mycophenolic Acid (Cellcept)FDA LinkGeneric
12/2008
1AntibodiesIBA
09/2003
1ConnectinIBA
09/2003

Therapy/Procedure

4Therapeutics
07/2022 - 09/2010
4Thymectomy
11/2020 - 11/2016
2Continuous Positive Airway Pressure
01/2022 - 03/2008
2Spinal Fusion (Spondylosyndesis)
01/2020 - 01/2018
2Noninvasive Ventilation
08/2018 - 10/2016
2Tracheostomy
10/2016 - 03/2008
1Positive-Pressure Respiration (Positive End-Expiratory Pressure)
02/2020
1Physical Therapy Modalities (Physical Therapy Technique)
01/2020
1Radiotherapy
01/2020
1Gastrostomy
08/2018
1Punctures
01/2018
1Mechanical Ventilators (Ventilator)
10/2016
1Complementary Therapies (Alternative Medicine)
06/2012